Camonsertib — Investigational Agent

Other · Phase 1/2 · Repare Therapeutics / Roche

Mechanism of Action

Camonsertib is a potent, orally bioavailable, selective inhibitor of ataxia telangiectasia and Rad3-related (ATR) kinase, a master regulator of the replication-stress response. In tumors harboring specific DNA damage response (DDR) alterations (e.g., ATM, BRCA1/2, RAD51C, CDK12), ATR inhibition abrogates cell-cycle checkpoint control and forces mitotic entry with unrepaired DNA, producing synthetic-lethal cell death. Camonsertib was engineered for high potency at low doses to widen its therapeutic index and enable tolerable combinations. It shows activity as monotherapy in molecularly…

Investigational Indications

Key Trials